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Federal
Detection of mutations in the dystrophin gene via automated DHPLC screening and direct sequencing
U.S. Department of Health & Human Services —
Background Currently molecular diagnostic laboratories focus only on the identification of large deletion and duplication mutations (spanning one exon or more) for... -
Federal
Size does matter: overcoming the adeno-associated virus packaging limit
U.S. Department of Health & Human Services —
Recombinant adeno-associated virus (rAAV) vectors mediate long-term gene transfer without any known toxicity. The primary limitation of rAAV has been the small size...